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In the overview the analysis of contemporary scientific researches in the area of medicamentous therapy of the genetical nervomuscular diseases is presented: the overview of spinal muscular atrophy and Duchenne muscular dystrophy has been carried out. Up to the present moment these diseases are incurable, but the common scientific work of geneticists, molecular biologists, clinicians, and pharmacologists gives promising prospects. Many researches are devoted to the question of elimination of the primary pathogenetic cause of these diseases with the usage of methods of the gene therapy.

M G Sokolova

North-Western State Medical University named after I.I. Mechnikov

O A Nikishina

North-Western State Medical University named after I.I. Mechnikov

M A Maretina

Research Institute of Obstetrics, Gynecology and Reproductology named after D.O. Ott

A V Kiselev

Research Institute of Obstetrics, Gynecology and Reproductology named after D.O. Ott

S V Lobzin

North-Western State Medical University named after I.I. Mechnikov

A A Zuev

North-Western State Medical University named after I.I. Mechnikov

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